Pediatric Clinical Trials: Open, Ongoing and Recruiting Studies
To inquire about current studies please contact us at:
NCRI.recruitment@nicklaushealth.orgPlaceholder Test
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Phase I/II Trial: Engineered Donor Graft (Orca Q) for Pediatric Hematopoietic Cell Transplant (HCT)Study ID:Principal Investigator:
Cardiology Clinical Trials
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PREEMIE: Study for Treatment of PDA in Premature Infants (PREEMIE)Study ID:Principal Investigator:
Dermatology Clinical Trials
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A Study to Evaluate the Pharmacokinetics, Safety, and Effectiveness of Certolizumab Pegol in Children With Moderate to Severe Chronic Plaque Psoriasis (CIMcare)Study ID:Principal Investigator:
Gastroenterology Clinical Trials
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Evaluation of Oral Tofacitinib in Children Aged 2 to 17 Years Old Suffering From Moderate to Severe Ulcerative ColitisStudy ID:Principal Investigator:
Nephrology Clinical Trials
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A Study of the Efficacy and Safety of DMX-200 in Patients With FSGS Who Are Receiving an ARB (ACTION3)Study ID:Principal Investigator:
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Study of Efficacy and Safety of Iptacopan in Participants With IC-MPGN (APPARENT)Study ID:Principal Investigator:
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Study of Efficacy and Safety of Iptacopan in Patients With C3 Glomerulopathy. (APPEAR-C3G)Study ID:Principal Investigator:
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Study of Sparsentan Treatment in Pediatrics With Proteinuric Glomerular Diseases (EPPIK)Study ID:Principal Investigator:
Neurology Clinical Trials
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A Double-blind Study Evaluating the Efficacy, Safety, and Tolerability of Zorevunersen in Patients With Dravet SyndromeStudy ID:Principal Investigator:
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A Study to Evaluate the Efficacy, Safety, and Tolerability of Brivaracetam as Monotherapy in Patients 2 to 25 Years of Age With Childhood Absence Epilepsy or Juvenile Absence Epilepsy (EXPAND)Study ID:Principal Investigator:
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A Study to Test the Long-term Safety and Tolerability of Brivaracetam in Study Participants With Childhood Absence Epilepsy or Juvenile Absence EpilepsyStudy ID:Principal Investigator:
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Blood Brain Barrier (BBB) Disruption Using Exablate Focused Ultrasound With Doxorubicin for Treatment of Pediatric Diffuse Intrinsic Pontine Gliomas (DIPG)Study ID:Principal Investigator:
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Efficacy and Safety of Erenumab in Pediatric Participants With Episodic Migraine (OASIS(EM))Study ID:Principal Investigator:
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Focal Cerebral Arteriopathy Steroid Trial (FOCAS)Study ID:Principal Investigator:
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Humanitarian Device Exemption (Dystonia IRB)Study ID:Principal Investigator:
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Phase 3 Efficacy and Safety Study of GTX-102 in Pediatric Subjects with AS (Aspire)Study ID:Principal Investigator:
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Randomized Study in Children and Adolescents With Migraine: Acute TreatmentStudy ID:Principal Investigator:
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Study to Assess the Efficacy, Safety, and Tolerability of Valbenazine for the Treatment of Dyskinesia Due to Cerebral PalsyStudy ID:Principal Investigator:
Orthopedics Clinical Trials
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Cast or Operation for Medial Epicondyle Fracture Treatment in Children (COMET)Study ID:Principal Investigator:
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Developmental Dysplasia of the Hip: Observation Vs. BracingStudy ID:Principal Investigator:
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Distal Radius Interventions for Fracture Treatment (DRIFT)Study ID:Principal Investigator:



